A little earlier than expected, Spark’s announces Luxturna pricing, $850k

RxC International has evaluated the Luxturna clinical story and its market opportunity, including critical questions regarding this highly-watched commercial launch.  Here's what you need to know.

Monthly Gene Therapy Business Review - December 2017

This month, the most noteworthy gene therapy stories include:

  • First Mover Advantage? Gilead Blazes Trail for Competition
  • Newly-Published Yescarta Study Raises Safety Concerns

  • Results from Hemophilia Gene Therapy Studies Prompt Pricing Questions...Again

Read about these developments and our commercial insights into the ongoing evolution of the gene therapy market.

Monthly Gene Therapy Business Review - November 2017

November saw some important moments in gene therapy.  We have summarized the most noteworthy and included the remaining in our news and updates sections.

Landmark Month Sees Second Gene Therapy Approved and Other Advances

October was a landmark month for gene therapies with the approval of the second-ever gene therapy in the US, Yescarta (axicabtagene ciloleucel) from Kite and Gilead.  The prior approval of Novartis’ Kymriah is more proof that gene therapies are set to shake up the pharma industry.  Gene therapies saw other wins as Luxturna, Spark’s treatment for Leber congenital amaurosis, received the FDA’s recommendation for approval and Bluebird Bio’s interim data report for its gene therapy Lenti-D to treat cerebral adrenoleukodystrophy showed promising results.

Planning for Gene Therapy Success

RxC Gene Therapy

With clinical trial successes bringing gene therapy closer to FDA approval and eventual commercialization, it's critical for companies developing gene therapies to understand the marketplace and plan accordingly.  

RxC International has put together a white paper containing important information on the current state of gene therapies, companies driving the market forward, and what to consider when beginning the process of commercialization.

Gene Therapy Articles and Other Resources